Gaucher Disease Research Highlights: WORLDSymposium 2022

Released On
April 15, 2022

Expires On
April 15, 2023

Media Type

Completion Time
15 minutes

Gastroenterology, Primary Care

Parkinson's & Movement Disorders

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This activity is jointly provided by American Academy of CME Inc. and CheckRare CE.

This activity is supported in part by an independent education grant from Takeda Pharmaceuticals U.S.A. Inc.

Credit Available

  • Physicians — maximum of 0.25 AMA PRA Category 1 Credit(s)

All other health care professionals completing this course will be issued a statement of participation.

Target Audience

This activity has been designed to meet the educational needs of physicians specializing in hematology/oncology, nephrology, gastroenterology, general practice/internal medicine. Other members of the care team may also participate.

Program Overview

At WORLDSymposium 2022, new information and data were presented on Gaucher disease—a rare lysosomal storage disease that results in a plethora of systemic problems—to help physicians learn more about the treatment options, new biomarkers, and the link between Gaucher disease and Parkinson’s disease.

This accredited CME activity highlights the latest information about Gaucher disease research and provides expert analysis of its clinical relevance for busy members of the care team in order to help them care for patients they may encounter with this rare condition.

Learning Objectives

Upon completion of this activity, participants should be better able to:

  • Describe the latest research being presented to better manage Gaucher disease and it clinical relevance.




Gregory Grabowski, MD

Professor Emeritus
University of Cincinnati College of Medicine
Departments of Pediatrics, and Molecular Genetics, Biochemistry and Microbiology
Division of Human Genetics
Cincinnati Children’s Hospital Research Foundation
Cincinnati, OH


Physician Accreditation Statement

In support of improving patient care, this activity has been planned and implemented by American Academy of CME, Inc. and CheckRare CE. American Academy of CME, Inc. is Jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.


Physician Credit Designation

American Academy of CME, Inc., designates this enduring material for a maximum of 0.25 AMA PRA Category 1 Credits™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Disclosures of Conflicts of Interest

According to the disclosure policy of the Academy, all faculty, planning committee members, editors, managers and other individuals who are in a position to control content are required to disclose any relationships with any ineligible company(ies). The existence of these relationships is not viewed as implying bias or decreasing the value of the activity. Clinical content has been reviewed for fair balance and scientific objectivity, and all of the relevant financial relationships listed for these individuals have been mitigated.

Disclosure of relevant financial relationships are as follows:

Gregory Grabowski, MD
  • Advisory Board/Consultant: Moderna SAB, Prevail Therapeutics SAB, Asklepios Biotherapeutics SAB, Vanqua Bio SAB, RallyBio, Shire/Takeda, Biai Biotech Investments (formerly Lysosomal Therapeutics)
  • Shareholder: Kiniksa Pharmaeuticals
  • Speakers Bureau: Shire/Takeda
  • Patent (Licensed): AstraZeneca/Shire/Takeda (Expired)

Planners for this activity have no relevant financial relationships with any commercial interests.

Instructions for Participation and Credit

There are no fees for participating and receiving CME credit for this enduring activity. To receive CME credit participants must:

  1. Read the CME/CE information and faculty disclosures.
  2. Participate in the online activity.
  3. Submit the evaluation form.
Certificates will be emailed to the participant

Course Viewing Requirements

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Google Chrome 28.0+ for Windows, Mac OS, or Linux
Mozilla Firefox 23.0+ for Windows, Mac OS, or Linux
Safari 6.0+ for Mac OSX 10.7 and above

Supported Phones & Tablets:
Android 4.0.3 and above
iPhone/iPad with iOS 6.1 or above

Disclosure of Unlabeled Use

American Academy of CME, Inc. requires that faculty participating in any CME activity disclose to the audience when discussing any unlabeled or investigational use of any commercial product or device not yet approved for use in the United States. This activity will review off-label or investigational information.


The opinions expressed in this educational activity are those of the faculty, and do not represent those of the Academy or CheckRare CE. This activity is intended as a supplement to existing knowledge, published information, and practice guidelines. Learners should appraise the information presented critically, and draw conclusions only after careful consideration of all available scientific information.

Contact Information

For CME questions please contact: